Editing aberrant splice sites efficiently restores beta-globin expression in beta-thalassemia.
Xu S, Luk K, Yao Q, Shen AH, Zeng J, Wu Y, Luo HY, Brendel C, Pinello L, Chui DHK, Wolfe SA, Bauer DE
Blood. 2019 Jan 31. pii: blood-2019-01-895094. doi: 10.1182/blood-2019-01-895094. PubMed Article
Xu S, Luk K, Yao Q, Shen AH, Zeng J, Wu Y, Luo HY, Brendel C, Pinello L, Chui DHK, Wolfe SA, Bauer DE
Blood. 2019 Jan 31. pii: blood-2019-01-895094. doi: 10.1182/blood-2019-01-895094. PubMed Article
Plasmids from Article
| ID | Plasmid | Purpose |
|---|---|---|
| 114366 | pET-21a_2xNLS_LbCpf1_protein_expression | Protein expression plasmid for 2xNLS LbCpf1 in pET-21a backbone |