In vivo base editing of Angptl3 via lipid nanoparticles to treat cardiovascular disease.
Khirallah J, Bloomer H, Wich D, Huang C, Workman JN, Li Y, Newby GA, Liu DR, Xu Q
Mol Ther Nucleic Acids. 2025 Feb 15;36(2):102486. doi: 10.1016/j.omtn.2025.102486. eCollection 2025 Jun 10.
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Plasmids from Article
| ID | Plasmid | Purpose |
|---|---|---|
| 221654 | pT7-ABE8e for IVT | Template plasmid for in vitro transcription (IVT) of adenine base editor ABE8e with SpCas9. |