Purpose
AAV production plasmid for HBA1 UTRs vector from Fig. 3 that mediates HDR at HBA1 locus using HBA1 sg5 gRNA. HBB gene includes introns; HBA1 UTRs flank HBA1 cassette. HAs are ~400bp each.
Insert
Hemoglobin Subunit Alpha 1 (
HBA1 Human)
Available since
April 18, 2025
Availability
Academic Institutions and Nonprofits only