pAAV-RHO-IntC-dCas9C-VPR-polyA Citations (2)

Originally described in: A gene therapy for inherited blindness using dCas9-VPR-mediated transcriptional activation.
Bohm S, Splith V, Riedmayr LM, Rotzer RD, Gasparoni G, Nordstrom KJV, Wagner JE, Hinrichsmeyer KS, Walter J, Wahl-Schott C, Fenske S, Biel M, Michalakis S, Becirovic E Sci Adv. 2020 Aug 19;6(34):eaba5614. doi: 10.1126/sciadv.aba5614. eCollection 2020 Aug. PubMed Journal

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Articles Citing pAAV-RHO-IntC-dCas9C-VPR-polyA

Articles
dCas9-VPR-mediated transcriptional activation of functionally equivalent genes for gene therapy. Riedmayr LM, Hinrichsmeyer KS, Karguth N, Bohm S, Splith V, Michalakis S, Becirovic E. Nat Protoc. 2022 Mar;17(3):781-818. doi: 10.1038/s41596-021-00666-3. Epub 2022 Feb 7. PubMed
Dual AAV vectors for efficient delivery of large transgenes. Mittas DM, Riedmayr LM, Gavrilov Z, Weber VJ, Otify DY, Mehlfeld V, Szalontai B, Ucambarlic E, Gandor C, Heigl T, Biel M, Becirovic E. Nat Protoc. 2025 Sep 11. doi: 10.1038/s41596-025-01243-8. PubMed

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