pJRH-1179 U6-reci Gag-Cas9 v2 Citations (1)
Originally described in: In vivo human T cell engineering with enveloped delivery vehicles.Hamilton JR, Chen E, Perez BS, Sandoval Espinoza CR, Kang MH, Trinidad M, Ngo W, Doudna JA Nat Biotechnol. 2024 Jan 11. doi: 10.1038/s41587-023-02085-z. PubMed Journal
Articles Citing pJRH-1179 U6-reci Gag-Cas9 v2
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Single-guide RNA Cas9 and enhanced-deletion Cas9 rescue a recurrent USH2A-related splicing defect. De Angeli P, Spaag S, Shliaga S, Flores-Tufino A, Ritter M, Nasri M, Stingl K, Kuhlewein L, Wissinger B, Kohl S. Mol Ther Nucleic Acids. 2025 Mar 21;36(2):102523. doi: 10.1016/j.omtn.2025.102523. eCollection 2025 Jun 10. PubMed |
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