An miRNA-mediated therapy for SCA6 blocks IRES-driven translation of the CACNA1A second cistron.

Miyazaki Y, Du X, Muramatsu S, Gomez CM
Sci Transl Med. 2016 Jul 13;8(347):347ra94. doi: 10.1126/scitranslmed.aaf5660. PubMed Article

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