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In utero gene editing for monogenic lung disease.

Alapati D, Zacharias WJ, Hartman HA, Rossidis AC, Stratigis JD, Ahn NJ, Coons B, Zhou S, Li H, Singh K, Katzen J, Tomer Y, Chadwick AC, Musunuru K, Beers MF, Morrisey EE, Peranteau WH
Sci Transl Med. 2019 Apr 17;11(488). pii: 11/488/eaav8375. doi: 10.1126/scitranslmed.aav8375. (Link opens in a new window) PubMed (Link opens in a new window) Article

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