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NHEJ-Mediated Repair of CRISPR-Cas9-Induced DNA Breaks Efficiently Corrects Mutations in HSPCs from Patients with Fanconi Anemia.

Roman-Rodriguez FJ, Ugalde L, Alvarez L, Diez B, Ramirez MJ, Risueno C, Corton M, Bogliolo M, Bernal S, March F, Ayuso C, Hanenberg H, Sevilla J, Rodriguez-Perales S, Torres-Ruiz R, Surralles J, Bueren JA, Rio P
Cell Stem Cell. 2019 Nov 7;25(5):607-621.e7. doi: 10.1016/j.stem.2019.08.016. Epub 2019 Sep 19. (Link opens in a new window) PubMed (Link opens in a new window) Article

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