Functionality of a bicistronic construction containing HEXA and HEXB genes encoding beta-hexosaminidase A for cell-mediated therapy of GM2 gangliosidoses.

Shaimardanova AA, Chulpanova DS, Solovyeva VV, Aimaletdinov AM, Rizvanov AA
Neural Regen Res. 2022 Jan;17(1):122-129. doi: 10.4103/1673-5374.314310. PubMed Article

Plasmids from Article

No plasmids are currently publicly available from Addgene for this article.