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Therapeutic homology-independent targeted integration in retina and liver.

Tornabene P, Ferla R, Llado-Santaeularia M, Centrulo M, Dell'Anno M, Esposito F, Marrocco E, Pone E, Minopoli R, Iodice C, Nusco E, Rossi S, Lyubenova H, Manfredi A, Di Filippo L, Iuliano A, Torella A, Piluso G, Musacchia F, Surace EM, Cacchiarelli D, Nigro V, Auricchio A
Nat Commun. 2022 Apr 12;13(1):1963. doi: 10.1038/s41467-022-29550-8. (Link opens in a new window) PubMed (Link opens in a new window) Article

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