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Rescue of lysosomal function as therapeutic strategy for SPG15 hereditary spastic paraplegia.

Vantaggiato C, Orso G, Guarato G, Brivio F, Napoli B, Panzeri E, Masotti S, Santorelli FM, Lamprou M, Gumeni S, Clementi E, Bassi MT
Brain. 2023 Mar 1;146(3):1103-1120. doi: 10.1093/brain/awac308. (Link opens in a new window) PubMed (Link opens in a new window) Article

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