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Adenine base editing efficiently restores the function of Fanconi anemia hematopoietic stem and progenitor cells.

Siegner SM, Ugalde L, Clemens A, Garcia-Garcia L, Bueren JA, Rio P, Karasu ME, Corn JE
Nat Commun. 2022 Nov 12;13(1):6900. doi: 10.1038/s41467-022-34479-z. (Link opens in a new window) PubMed (Link opens in a new window) Article

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