AAV-mediated interneuron-specific gene replacement for Dravet syndrome.
Mich JK, Ryu J, Wei AD, Gore BB, Guo R, Bard AM, Martinez RA, Bishaw Y, Luber E, Oliveira Santos LM, Miranda N, Ramirez JM, Ting JT, Lein ES, Levi BP, Kalume FK
bioRxiv [Preprint]. 2023 Dec 15:2023.12.15.571820. doi: 10.1101/2023.12.15.571820.
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