Adenine base editing-mediated exon skipping restores dystrophin in humanized Duchenne mouse model.
Lin J, Jin M, Yang D, Li Z, Zhang Y, Xiao Q, Wang Y, Yu Y, Zhang X, Shao Z, Shi L, Zhang S, Chen WJ, Wang N, Wu S, Yang H, Xu C, Li G
Nat Commun. 2024 Jul 15;15(1):5927. doi: 10.1038/s41467-024-50340-x.
(Link opens in a new window)
PubMed
(Link opens in a new window)
Article
Plasmids from Article
No plasmids are currently publicly available from Addgene for this article.