Genomic safe harbors permit high β-globin transgene expression in thalassemia induced pluripotent stem cells.
Papapetrou EP, Lee G, Malani N, Setty M, Riviere I, Tirunagari LM, Kadota K, Roth SL, Giardina P, Viale A, Leslie C, Bushman FD, Studer L, Sadelain M
Nat Biotechnol. 2011 Jan;29(1):73-8. doi: 10.1038/nbt.1717. Epub 2010 Dec 12.
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Plasmids from Article
| ID | Plasmid | Purpose |
|---|---|---|
| 27512 | pLM-fSV2A | |
| 27546 | pLM-CMV-R-Cre | Lentiviral bicistronic co-expression of Cre and mCherry; linked by a P2A peptide. |