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We narrowed to 7,855 results for: aav

Showing: 7441 - 7460 of 7855 results
  1. PRINCE-SaCas9-2

    Plasmid
    #250958
    Purpose
    PRINCE drug inducible gene editing system based on SaCas9 (AAV-Part II : the expression of 2x ERT2 and the sgRNA is under drug-mediated control)
    Depositor
    Insert
    H1-TetO-SaCas9 sgRNA scaffold; EF1α-NpuC; 2×ERT2; opTtetR; GFP
    Use
    AAV and CRISPR
    Expression
    Mammalian
    Promoter
    H1 promoter; EF1α promoter
    Available Since
    July 2, 2026
    Availability
    Academic Institutions and Nonprofits only
  2. MKC175_HBA1reg(synEPOR)

    Plasmid
    #232413
    Purpose
    AAV production plasmid for HBA1 UTRs vector from Fig. 3 that mediates HDR at HBA1 locus using HBA1 sg5 gRNA. HBB gene includes introns; HBA1 UTRs flank H+C15BA1 cassette. HAs are ~400bp each.
    Depositor
    Insert
    Truncated Erythropoietin Receptor (EPOR Human)
    Use
    AAV
    Expression
    Mammalian
    Available Since
    April 18, 2025
    Availability
    Academic Institutions and Nonprofits only
  3. MKC176_EPOR(2A-synEPOR)

    Plasmid
    #232414
    Purpose
    AAV production plasmid for EPOR(synEPOR) vector from Figs. 3-5 that mediates HDR at EPOR locus using EPOR gRNA. synEPOR is codon diverged to prevent premature recombination with EPOR locus.
    Depositor
    Insert
    Truncated Erythropoietin Receptor (EPOR Human)
    Use
    AAV
    Expression
    Mammalian
    Available Since
    Feb. 27, 2025
    Availability
    Academic Institutions and Nonprofits only
  4. MKC91_tEPOR(UbC-GFP-BGH)

    Plasmid
    #232406
    Purpose
    AAV production plasmid for tEPOR-UbC-GFP-BGH vector from Fig. 1 that mediates HDR at EPOR locus using EPOR-sg1 gRNA. Repair vector introduces premature stop codon into EPOR locus.
    Insert
    Truncated Erythropoietin Receptor (EPOR Human)
    Use
    AAV
    Expression
    Mammalian
    Available Since
    Feb. 26, 2025
    Availability
    Academic Institutions and Nonprofits only
Showing: 7441 - 7460 of 7855 results