CRISPR in the Clinic
Type
Blog Post
...alternatively be harvested, edited ex vivo, and then returned to the patient. Finally, allogenic therapies involve...approach, editing patient cells ex vivo and then returning them to the patient.
The first human trial involving...clinical trial for SCD in 2022 as well.
Hereditary transthyretin amyloidosis (hATTR)
hATTR is caused by a variety...