Purpose
AAV production plasmid for HBA+tEPOR vector from Figs. 4-6 that mediates HDR at HBB locus using HBB sg7 gRNA. HBA gene includes HBA1 exons and introns; HBA1 UTRs flank HBA+tEPOR cassette.
Insert
Hemoglobin Subunit Alpha 1 (
HBA1 Human)
Available Since
April 18, 2025
Availability
Academic Institutions and Nonprofits only