KRD2_HBA1(HBA1reg-UbC-GFP)
Plasmid
#232401
Purpose
AAV production plasmid for HBA1 WGR vector from Fig. 1 that mediates HDR at HBA1 locus using HBA1 sg5 gRNA. HBA1 UTRs flank UbC-GFP cassette; GFP is followed by BGH polyA. HAs are ~400bp each.
Depositor
Available Since
Feb. 26, 2025
Availability
Academic Institutions and Nonprofits only