KRD22_HBA1(HBA1reg-HBB-longHAs)
Plasmid
#232403
Purpose
AAV production plasmid for HBA1 long HAs vector from Figs. 3-6 that mediates HDR at HBA1 locus using HBA1 sg5 gRNA. HBB gene includes introns; HBA1 UTRs flank full HBA1-2A-YFP cassette. HAs are ~900bp
Depositor
Use
Tags
Expression
Mammalian
Mutation
Promoter
Available since
April 18, 2025
Availability
Academic Institutions and Nonprofits only